Abstract
Primary microcephaly is a genetically heterogeneous condition characterized by reduced head circumference (-3 SDS or more) and mild-to-moderate learning disability. Here, we describe clinical and molecular investigations of a microcephalic child with sensorineural hearing loss. Although consanguinity was unreported initially, detection of 13.7 Mb of copy neutral loss of heterozygosity (cnLOH) on chromosome 9 implicated the CDK5RAP2 gene. Targeted sequencing identified a homozygous E234X mutation, only the third mutation to be described in CDK5RAP2, the first in an individual of non-Pakistani descent. Sensorineural hearing loss is not generally considered to be consistent with autosomal recessive microcephaly and therefore it seems likely that the deafness in this individual is caused by the co-occurrence of a further gene mutation, independent of CDK5RAP2. Nevertheless, further detailed clinical descriptions of rare CDK5RAP2 patients, including hearing assessments will be needed to resolve fully the phenotypic range associated with mutations in this gene. This study also highlights the utility of SNP-array testing to guide disease gene identification where an autosomal recessive condition is plausible.
MeSH Terms
Cell Cycle Proteins
Child
Codon, Nonsense
Female
Hearing Loss, Sensorineural/genetics
Humans
Intracellular Signaling Peptides and Proteins/genetics
Microcephaly/genetics
Nerve Tissue Proteins/genetics
Pedigree
Polymorphism, Single Nucleotide
Sequence Analysis, DNA
Somalia
Chemicals
CDK5RAP2 protein, human
Cell Cycle Proteins
Codon, Nonsense
Intracellular Signaling Peptides and Proteins
Nerve Tissue Proteins
Authors & Affiliations
13 authors, click to expand affiliations / ORCID
Pagnamenta Alistair T
NIHR Biomedical Research Centre, Oxford and Wellcome Trust Centre for Human Genetics, University of Oxford, UK.
Murray Jennie E
Yoon Grace
Sadighi Akha Elham
Harrison Victoria
Bicknell Louise S
Ajilogba Kaseem
Stewart Helen
Kini Usha
Taylor Jenny C
Keays David A
Jackson Andrew P
Knight Samantha J L
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