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PMID: 820173 Published · ppublish English Journal Article

Enzyme replacement therapy for the sphingolipidoses.

Advances in experimental medicine and biology ·Vol. 68 ·1976-00-00 ·Pages 523-32

Brady RO, Pentchev PG, Gal AE, Hibbert SR, Quirk JM, Mook GE, Kusiak JW, Tallman JF, Dekaban AS

Abstract

暂无摘要

MeSH Terms
Ceramides Cerebrosides/metabolism Galactosylgalactosylglucosylceramidase/therapeutic use Gaucher Disease/drug therapy,metabolism Glucosylceramidase/therapeutic use Glycoside Hydrolases/therapeutic use Humans Lipidoses/drug therapy Liver/metabolism Sphingolipidoses/drug therapy Time Factors
Chemicals
Ceramides Cerebrosides Glycoside Hydrolases Glucosylceramidase Galactosylgalactosylglucosylceramidase
Authors & Affiliations
9 authors, click to expand affiliations / ORCID
Brady R O
Pentchev P G
Gal A E
Hibbert S R
Quirk J M
Mook G E
Kusiak J W
Tallman J F
Dekaban A S
Article Info
Journal
Advances in experimental medicine and biology
Abbr.
Adv Exp Med Biol
ISSN
0065-2598
Published
1976-00-00
Pages
523-32
Language
English
Region
United States
NLM ID
0121103
Subset
IM
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